\u672c\u9662\u5206\u5b50\u751f\u7269\u7814\u7a76\u6240\u9673\u4fca\u5b89\u526f\u7814\u7a76\u54e1\u9818\u5c0e\u7684\u7814\u7a76\u5718\u968a\uff0c\u8207\u9ad8\u96c4\u91ab\u5b78\u5927\u5b78\u9418\u80b2\u5fd7\u8b1b\u5ea7\u6559\u6388\u7814\u7a76\u5718\u968a\u5408\u4f5c\uff0c\u767c\u73fe\u4e00\u500b\u5fae\u578b\u6838\u7cd6\u6838\u9178\u5bb6\u65cf\u300cmicroRNA-34\u300d\u6216\u300cMiR34\u300d\u6703\u53c3\u8207\u810a\u9ad3\u6027\u808c\u8089\u840e\u7e2e\u75c7\uff08Spinal muscular atrophy, SMA\uff09\u7684\u75c5\u7a0b\u767c\u5c55\uff0c\u4e14\u6709\u6f5b\u529b\u4f5c\u70ba\u8a55\u4f30\u810a\u9ad3\u6027\u808c\u8089\u840e\u7e2e\u75c7\u6cbb\u7642\u7642\u6548\u7684\u81e8\u5e8a\u751f\u7269\u6a19\u8a18\u3002\u6b64\u4e00\u767c\u73fe\u70ba\u5c0f\u6838\u7cd6\u6838\u9178\u5982\u4f55\u5f71\u97ff SMA \u75c5\u7406\u8b8a\u5316\u63d0\u4f9b\u4e86\u5d84\u65b0\u7684\u898b\u89e3\uff0c\u4e26\u53ef\u70ba SMA \u7684\u6cbb\u7642\u5e36\u4f86\u66f4\u5468\u5168\u7684\u6cbb\u7642\u6548\u76ca\u3002\u6b64\u9805\u7814\u7a76\u8fd1\u671f\u5df2\u767c\u8868\u65bc\u570b\u969b\u671f\u520a\u300a\u5206\u5b50\u6cbb\u7642 – \u6838\u9178\u300b\uff08Molecular Therapy – Nucleic Acids<\/em>\uff09\uff0c\u4e26\u5df2\u7533\u8acb\u7f8e\u570b\u5c08\u5229\u512a\u5148\u6b0a\u3002<\/p>\n
\u6b64\u7814\u7a76\u7372\u5f97\u672c\u9662\u3001\u9ad8\u96c4\u91ab\u5b78\u5927\u5b78\u4ee5\u53ca\u9ad8\u91ab\u5927\u9644\u8a2d\u4e2d\u548c\u7d00\u5ff5\u91ab\u9662\u3001\u570b\u5bb6\u885b\u751f\u7814\u7a76\u9662\u3001\u570b\u5bb6\u79d1\u5b78\u53ca\u6280\u8853\u59d4\u54e1\u6703\u7684\u8cc7\u52a9\u3002<\/p>\n
\u7814\u7a76\u8aaa\u660e\uff1a https:\/www.imb.sinica.edu.tw\/en\/research\/publication_show.php?pid=230<\/a>
\n\u7814\u7a76\u8ad6\u6587\uff1a https:\/doi.org\/10.1016\/j.omtn.2023.03.005<\/a><\/p>\n